Rare Diseases

Health & Wellness 4 min The First Approved Drug for MCT8 Deficiency Treats the Body's Excess Hormone, Not the Brain The FDA approved Egetis's Emcitate (tiratricol) on 28 September. It lowers the thyroid hormone that builds up... AM Amelia Wong 30 Sep Health & Wellness 4 min The FDA Approved a Third Drug for a Disease That Turns Muscle Into Bone Atebrioz joins two earlier treatments for fibrodysplasia ossificans progressiva, one approved five weeks ago.... AM Amelia Wong 27 Sep